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Tag: Niemann Pick Disease

November 2, 2020 CD as API / Pharma applications

Treatment of Niemann-Pick Disease Type C using crosslinked 2-hydroxypropyl-β-cyclodextrin

Niemann-Pick Disease Type C (NPC) is a severe neurovisceral disorder that is pathophysiologically characterized by intracellular transport abnormalities leading to

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September 9, 2020 CD as API / CD derivatives / Pharma applications

Cyclo Therapeutics Announces Data from Ongoing Niemann-Pick Disease Type C1 (NPC1) Trial

Cyclo Therapeutics, a clinical stage biotechnology company that develops cyclodextrin-based products for the treatment of Niemann-Pick Disease Type C (NPC)

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September 7, 2020 CD as API / Pharma applications

Potential COVID-19 therapeutics from a rare disease: utilization of lipid dysregulation to combat viral infectivity

Strategic drug repurposing in combination with rapid testing of established molecular targets could provide a pause in disease progression and

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May 15, 2020 CD as API / Pharma applications

Cyclo Therapeutics reports international patent application for treating Alzheimer’s

Cyclo Therapeutics reported the publication of an international patent application for the treatment of Alzheimer’s disease with HPBCD.

March 16, 2020 CD as API / CD derivatives

pH-Responsive Polymersome Microparticles as Smart Cyclodextrin-Releasing Agents

A paper has recently come out open-access in Biomacromolecules reporting on pH-Responsive Polymersome Microparticles as Smart Cyclodextrin-Releasing Agents (DOI: 10.1021/acs.biomac.9b01083).

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February 6, 2020 CD as API / CD derivatives / Pharma applications / Uncategorized

Cyclo Therapeutics Presents Clinical Trial Data on Niemann-Pick Type C Disease

Cyclo Therapeutics, Inc. a clinical-stage biotechnology company that develops cyclodextrin-based products for the treatment of Niemann-Pick Disease Type C (NPC)

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October 25, 2019 CD as API / CD derivatives / Pharma applications

Cyclo Therapeutics Announces Completion of Enrollment in its Phase I Trial to Evaluate Trappsol® Cyclo™ for the Treatment of Niemann-Pick Disease Type C

Cyclo Therapeutics, Inc. formerly CTD Holdings, Inc., a biotechnology company that develops cyclodextrin-based products for the treatment of disease, announced

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September 4, 2019 Drug delivery / Pharma applications

HPBCD is the active component in a triple combination formulation for treatment of Niemann-Pick C1 disease

Niemann-Pick type C1 (NPC1) disease is a fatal neurovisceral disease for which there are no FDA approved treatments, though cyclodextrin

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July 9, 2019 CD as API / Events / Pharma applications

National Niemann Pick Disease Family Conference

The annual National Niemann Pick Disease Family Conference will be held on August 15-18, 2019, in Bloomington, US. The conference

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May 30, 2019 CD as API / CD derivatives

Lactosyl-β-cyclodextrin against Hepatomegaly in Niemann-Pick Type C Disease

The first paper in the special issue of Nanomaterials “Nanoconstructs Based on Cyclodextrins” has been published. Mono-lactosyl β-CD (mono-Lac-β-CD) diminished

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  • Cyclodextrin-Branched Polymer Releasing Nitric Oxide with Fluorescent Self-Reporting and Its Combination with Doxorubicin
  • Innovative Titanium Coatings for Enhanced Dental Implants
  • Bio-inks for skin regeneration: phase-adaptive design, multifunctional platforms, and 4D bioprinting frontiers
  • FermenGIN: γ-Cyclodextrin Takes the Bitterness Out of Bioconverted Red Ginseng
  • New book on beta-cyclodextrin and its derivatives

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Top Posts

  • Innovative Titanium Coatings for Enhanced Dental Implants
  • Cyclodextrin-Branched Polymer Releasing Nitric Oxide with Fluorescent Self-Reporting and Its Combination with Doxorubicin
  • Bio-inks for skin regeneration: phase-adaptive design, multifunctional platforms, and 4D bioprinting frontiers
  • New cyclodextrin with orphan drug designation: SBECD
  • Cyclodextrin dimers to treat atherosclerotic plaques by targeting various forms of cholesterol
  • Cyclarity Unveils First-Ever Clinical Data Demonstrating Excretion of Oxidized Cholesterol, at American Heart Association Vascular Discovery Scientific Sessions
  • Old but Gold (literally)!
  • Lanosterol eye drops for cataract treatment
  • Selecting a non-interacting buffer for α-cyclodextrin containing solutions
  • International Summer School on Cyclodextrins

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